Addressing issues in conducting clinical trials for rare diseases

Simon Ng — Thu, 03 Feb 2022 12:25:09 +0000

Will Chou, MD, Aruvant, New York, NY, gives an overview of challenges associated with conducting clinical trials for rare and orphan diseases such as sickle cell disease (SCD) and hypophosphatasia. Due the nature of these diseases, finding an adequate number of patients can be a barrier and Dr Chou additionally highlights the need to collaborate with patients groups to educate and build rapport with them for successful clinical trial recruitment. This interview took place at Advanced Therapies Week 2022.

Hypophosphatasia – VJRegenMed

Addressing issues in conducting clinical trials for rare diseases